Experimental Hematology
Volume 36, Issue 11 , Pages 1428-1435 , November 2008

Gene therapy of Diamond Blackfan anemia CD34+ cells leads to improved erythroid development and engraftment following transplantation

  • Johan Flygare

      Affiliations

    • Department of Molecular Medicine and Gene Therapy, Lund Stem Cell Center, Lund University Hospital, Lund, Sweden
    • Whitehead Institute for Biomedical Research, Massachusetts Institute of Technology, Cambridge, Mass., USA
    • Corresponding Author InformationOffprint requests to: Johan Flygare, M.D., Ph.D., Whitehead Institute for Biomedical Research, Massachusetts Institute of Technology, 9 Cambridge Center, Cambridge, MA 02142
    • ,
  • Karin Olsson

      Affiliations

    • Department of Molecular Medicine and Gene Therapy, Lund Stem Cell Center, Lund University Hospital, Lund, Sweden
    • ,
  • Johan Richter

      Affiliations

    • Department of Molecular Medicine and Gene Therapy, Lund Stem Cell Center, Lund University Hospital, Lund, Sweden
    • ,
  • Stefan Karlsson

      Affiliations

    • Department of Molecular Medicine and Gene Therapy, Lund Stem Cell Center, Lund University Hospital, Lund, Sweden

Received 21 May 2008 ,Revised 16 June 2008 ,Accepted 24 June 2008.

References 

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PII: S0301-472X(08)00310-X

doi: 10.1016/j.exphem.2008.06.012

Experimental Hematology
Volume 36, Issue 11 , Pages 1428-1435 , November 2008

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